A Phase I, Safety and Pharmacokinetics/pharmacodynamics Study of Oral L-CIT Supplementation in Preterm Infants with BPD±PH and NEC

Status: Recruiting
Location: See location...
Intervention Type: Dietary supplement
Study Type: Interventional
Study Phase: Not Applicable
SUMMARY

The purpose of this study is to evaluate the safety and explore the PK/PD of L-CIT supplementation in preterm infants to prevent the development of inflammatory pathways initiated by low levels of plasma CIT, specifically in preterm infants with post surgical NEC and BPD±PH.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 1 month
Maximum Age: 6 months
Healthy Volunteers: f
View:

• Born ≤ 30 weeks at birth

• Post-menstrual age (PMA) ≥ 34 weeks

• Echocardiographic evidence of PH for infants with BPD+PH

• On invasive or non-invasive ventilation with RSS \>2.0 for \>12hours/day for at least 48 hours

• Informed written consent (parents/substitute decision maker)

• Born ≤ 30 weeks at birth

• Recovering from Stage IIIb NEC as per modified Bell's staging (pneumoperitoneum requiring surgery)

• Tolerating 30 ml/kg/day of enteral feeds

• On invasive or non-invasive ventilation (NIPPV/nCPAP) with RSS \>2.0 for \> 12hours/day for at least 48 hours, 10-14 days post surgery

• Informed written consent (parents/substitute decision maker)

• Considered medically stable by clinical team

Locations
Other Locations
Canada
The Hospital For Sick Children
RECRUITING
Toronto
Contact Information
Primary
Rachana Patel, MSc, CCRP
rachana.patel@sickkids.ca
+1(416)-813-7654
Backup
Rosanna Yankanah, MSc, CCRP
rosanna.yankanah@sickkids.ca
+1(416-)813-7654
Time Frame
Start Date: 2023-11-01
Estimated Completion Date: 2028-03
Participants
Target number of participants: 60
Treatments
Experimental: BPD±PH
Arm 1: BPD±PH~Total of 12-24 infants; 6-12 at each dose level of oral dosage form of L-Citrulline. (300 or 500 mg/kg/day divided q6 hours).~Dose Level 1 = 300 mg/kg/day Dose Level 2 = 500 mg/kg/day
Experimental: Surgical NEC
Arm 2: sNEC~A total of 18-36 infants with Stage III NEC; 6-12 at each dose level of oral dosage form of L-Citrulline. (75, 150 or 225 mg/kg/day divided q6 hours)~Dose Level 1 = 75 mg/kg/day Dose Level 2 = 150 mg/kg/day Dose Level 3 = 225 mg/kg/day
Sponsors
Leads: The Hospital for Sick Children

This content was sourced from clinicaltrials.gov